The company supports its patients with rare diseases in advocating health insurance exchanges to: recognize rare diseases; include adequate number of in-network providers and allow patients with extremely rare diseases access to out-of-network providers without incurring excessive costs; access to all medically necessary therapies; access to all sites of care determined by healthcare provider and patient; ensure cost sharing does not discriminate or unfairly target any patient or rare disease group; access to third party cost sharing (premium, co-pay and co-insurance) assistance and due process and transparency to management utilization and medical necessity determinations, appeals and grievances.